Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics

Por Chen, Jennifer CJ, King, Oliver D, Zhang, Yuanfan, Clayton, Nicholas P, Spencer, Carrie, Wentworth, Bruce M, Emerson, Charles P, Wagner, Kathryn R
Publicado no Mol Ther (2016)

Dimorphic effects of TGFβ signaling during aortic aneurysm progression in mice suggest a combinatorial therapy for Marfan syndrome

Por Cook, Jason R., Clayton, Nicholas P., Carta, Luca, Galatioto, Josephine, Chiu, Emily, Smaldone, Silvia, Nelson, Carol A., Cheng, Seng H., Wentworth, Bruce M., Ramirez, Francesco
Publicado no Arterioscler Thromb Vasc Biol (2015)

Antisense Oligonucleotide-mediated Suppression of Muscle Glycogen Synthase 1 Synthesis as an Approach for Substrate Reduction Therapy of Pompe Disease

Por Clayton, Nicholas P, Nelson, Carol A, Weeden, Timothy, Taylor, Kristin M, Moreland, Rodney J, Scheule, Ronald K, Phillips, Lucy, Leger, Andrew J, Cheng, Seng H, Wentworth, Bruce M
Publicado em 2014

Inhibiting TGF-β Activity Improves Respiratory Function in mdx Mice

Por Nelson, Carol A., Hunter, R. Bridge, Quigley, Lindsay A., Girgenrath, Stefan, Weber, William D., McCullough, Jennifer A., Dinardo, Carol J., Keefe, Kelly A., Ceci, Lorena, Clayton, Nicholas P., McVie-Wylie, Alison, Cheng, Seng H., Leonard, John P., Wentworth, Bruce M.
Publicado em 2011