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Generation of isogenic Propionyl-CoA carboxylase beta subunit (PCCB) deficient induced pluripotent stem cell lines

Propionic acidemia (PA) is an autosomal recessive metabolic liver disease caused by defects in propionyl CoA carboxylase. Propionyl CoA carboxylase is a dodecameric enzyme consisting of multiple copies of alpha and beta subunits encoded by the PCCA and PCCB genes. Mutations in either PCCA or PCCB ca...

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Detalhes bibliográficos
Publicado no:Stem Cell Res
Main Authors: Pournasr, Behshad, Duncan, Stephen A.
Formato: Artigo
Idioma:Inglês
Publicado em: 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7640943/
https://ncbi.nlm.nih.gov/pubmed/32822967
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.scr.2020.101953
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