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Desmosterolosis presenting with multiple congenital anomalies

Desmosterolosis is a rare multiple congenital anomaly syndrome caused by a defect in the enzyme 3-beta-hydroxysterol delta-24-reductase (DHCR24) in the cholesterol biosynthesis pathway. Defects in this enzyme cause increased level of the cholesterol precursor desmosterol while disrupting development...

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Dades bibliogràfiques
Publicat a:Eur J Med Genet
Autors principals: Rohanizadegan, Mersedeh, Sacharow, Stephanie
Format: Artigo
Idioma:Inglês
Publicat: 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5963269/
https://ncbi.nlm.nih.gov/pubmed/29175559
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ejmg.2017.11.009
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