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Brain RNA-Seq Profiling of the Mucopolysaccharidosis Type II Mouse Model

Lysosomal storage disorders (LSDs) are a group of about 50 genetic metabolic disorders, mainly affecting children, sharing the inability to degrade specific endolysosomal substrates. This results in failure of cellular functions in many organs, including brain that in most patients may go through pr...

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Podrobná bibliografie
Vydáno v:Int J Mol Sci
Hlavní autoři: Salvalaio, Marika, D’Avanzo, Francesca, Rigon, Laura, Zanetti, Alessandra, D’Angelo, Michela, Valle, Giorgio, Scarpa, Maurizio, Tomanin, Rosella
Médium: Artigo
Jazyk:Inglês
Vydáno: MDPI 2017
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5454982/
https://ncbi.nlm.nih.gov/pubmed/28513549
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms18051072
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