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Progress and potential of non-inhibitory small molecule chaperones for the treatment of Gaucher disease and its potential implications for Parkinson disease

Gaucher disease, caused by pathological mutations GBA1, encodes the lysosome-resident enzyme glucocerebrosidase, which cleaves glucosylceramide into glucose and ceramide. In Gaucher disease, glucocerebrosidase deficiency leads to lysosomal accumulation of substrate, primarily in cells of the reticul...

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Detalles Bibliográficos
Publicado en:Expert Rev Proteomics
Autores principales: Jung, Olive, Patnaik, Samarjit, Marugan, Juan, Sidransky, Ellen, Westbroek, Wendy
Formato: Artigo
Lenguaje:Inglês
Publicado: 2016
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC5381920/
https://ncbi.nlm.nih.gov/pubmed/27098312
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1080/14789450.2016.1174583
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