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Putzeist, Michelle, Aukje K. Mantel-Teeuwisse, Christine C Gispen-de Wied, Arno W. Hoes, Hubert GM Leufkens, und Remco LA de Vrueh. Drug Development for Exceptionally Rare Metabolic Diseases: Challenging but Not Impossible. BioMed Central, 2013.

Putzeist, Michelle, et al. Drug Development for Exceptionally Rare Metabolic Diseases: Challenging but Not Impossible. BioMed Central, 2013.