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Alternative Splicing as a Therapeutic Target for Human Diseases

The majority of eukaryotic genes undergo alternative splicing, an evolutionarily conserved phenomenon, to generate functionally diverse protein isoforms from a single transcript. The fact that defective pre-mRNA splicing can generate non-functional and often toxic proteins with catastrophic effects,...

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Autors principals: Dery, Kenneth J., Gusti, Veronica, Gaur, Shikha, Shively, John E., Yen, Yun, Gaur, Rajesh K.
Format: Artigo
Idioma:Inglês
Publicat: 2009
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3076216/
https://ncbi.nlm.nih.gov/pubmed/19495693
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-1-60327-295-7_10
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