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Inhibition of MicroRNA 6937 Delays Photoreceptor and Vision Loss in a Mouse Model of Retinitis Pigmentosa

Inherited retinal dystrophies (IRDs) are a group of rare retinal conditions, including retinitis pigmentosa (RP), caused by monogenic mutations in 1 out of more than 250 genes. Despite recent advancements in gene therapy, there is still a lack of an effective treatment for this group of retinal cond...

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Autores principales: Ander Anasagasti, Araceli Lara-López, Santiago Milla-Navarro, Leire Escudero-Arrarás, María Rodríguez-Hidalgo, Nerea Zabaleta, Gloria González Aseguinolaza, Pedro de la Villa, Javier Ruiz-Ederra
Formato: Artigo
Lenguaje:Inglês
Publicado: MDPI AG 2020-09-01
Colección:Pharmaceutics
Materias:
miR
IRD
Acceso en línea:https://www.mdpi.com/1999-4923/12/10/913
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