Therapeutic impact of systemic AAV-mediated RNA interference in a mouse model of myotonic dystrophy

door Bisset, Darren R., Stepniak-Konieczna, Ewa A., Zavaljevski, Maja, Wei, Jessica, Carter, Gregory T., Weiss, Michael D., Chamberlain, Joel R.
Gepubliceerd in Hum Mol Genet (2015)