New functionalities in Orphanet for orphan drugs, R&D and marketing authorisations to better serve the rare diseases community

Yazar: Hivert, Virginie, Martin, Natalia, Hanauer, Marc, Aymé, Ségolène
Baskı/Yayın Bilgisi 2010

Rare diseases research in Europe: an overview based on data from the Orphanet database

Yazar: Martin, Natalia, Doulet, Nicolas, Hivert, Virginie, Aymé, Ségolène
Baskı/Yayın Bilgisi 2010

Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group

Yazar: Gahl, William A., Wong-Rieger, Durhane, Hivert, Virginie, Yang, Rachel, Zanello, Galliano, Groft, Stephen
Yayımlandı Orphanet J Rare Dis (2021)

The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases – recommendations of the IRDiRC Data Mining...

Yazar: Southall, Noel T, Natarajan, Madhusudan, Lau, Lilian Pek Lian, Jonker, Anneliene Hechtelt, Deprez, Benoît, Guilliams, Tim, Hunter, Lawrence, Rademaker, Carin MA, Hivert, Virginie, Ardigò, Diego
Yayımlandı Orphanet J Rare Dis (2019)

Barriers to the conduct of randomised clinical trials within all disease areas

Yazar: Djurisic, Snezana, Rath, Ana, Gaber, Sabrina, Garattini, Silvio, Bertele, Vittorio, Ngwabyt, Sandra-Nadia, Hivert, Virginie, Neugebauer, Edmund A. M., Laville, Martine, Hiesmayr, Michael, Demotes-Mainard, Jacques, Kubiak, Christine, Jakobsen, Janus C., Gluud, Christian
Yayımlandı Trials (2017)

Evaluating the “return on patient engagement initiatives” in medicines research and development: A literature review

Yazar: Vat, Lidewij Eva, Finlay, Teresa, Jan Schuitmaker‐Warnaar, Tjerk, Fahy, Nick, Robinson, Paul, Boudes, Mathieu, Diaz, Ana, Ferrer, Elisa, Hivert, Virginie, Purman, Gabor, Kürzinger, Marie‐Laure, Kroes, Robert A., Hey, Claudia, Broerse, Jacqueline E.W.
Yayımlandı Health Expect (2019)

Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective

Yazar: Dawkins, Hugh J.S., Draghia‐Akli, Ruxandra, Lasko, Paul, Lau, Lilian P.L., Jonker, Anneliene H., Cutillo, Christine M., Rath, Ana, Boycott, Kym M., Baynam, Gareth, Lochmüller, Hanns, Kaufmann, Petra, Le Cam, Yann, Hivert, Virginie, Austin, Christopher P.
Yayımlandı Clin Transl Sci (2017)

A systematic literature review of evidence-based clinical practice for rare diseases: what are the perceived and real barriers for improving the evidence and how can they be overco...

Yazar: Rath, Ana, Salamon, Valérie, Peixoto, Sandra, Hivert, Virginie, Laville, Martine, Segrestin, Berenice, Neugebauer, Edmund A. M., Eikermann, Michaela, Bertele, Vittorio, Garattini, Silvio, Wetterslev, Jørn, Banzi, Rita, Jakobsen, Janus C., Djurisic, Snezana, Kubiak, Christine, Demotes-Mainard, Jacques, Gluud, Christian
Yayımlandı Trials (2017)

Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective

Yazar: Austin, Christopher P., Cutillo, Christine M., Lau, Lilian P.L., Jonker, Anneliene H., Rath, Ana, Julkowska, Daria, Thomson, David, Terry, Sharon F., de Montleau, Béatrice, Ardigò, Diego, Hivert, Virginie, Boycott, Kym M., Baynam, Gareth, Kaufmann, Petra, Taruscio, Domenica, Lochmüller, Hanns, Suematsu, Makoto, Incerti, Carlo, Draghia‐Akli, Ruxandra, Norstedt, Irene, Wang, Lu, Dawkins, Hugh J.S.
Yayımlandı Clin Transl Sci (2017)