New functionalities in Orphanet for orphan drugs, R&D and marketing authorisations to better serve the rare diseases community

von Hivert, Virginie, Martin, Natalia, Hanauer, Marc, Aymé, Ségolène
Veröffentlicht 2010

Rare diseases research in Europe: an overview based on data from the Orphanet database

von Martin, Natalia, Doulet, Nicolas, Hivert, Virginie, Aymé, Ségolène
Veröffentlicht 2010

Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group

von Gahl, William A., Wong-Rieger, Durhane, Hivert, Virginie, Yang, Rachel, Zanello, Galliano, Groft, Stephen
Veröffentlicht in Orphanet J Rare Dis (2021)

The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases – recommendations of the IRDiRC Data Mining...

von Southall, Noel T, Natarajan, Madhusudan, Lau, Lilian Pek Lian, Jonker, Anneliene Hechtelt, Deprez, Benoît, Guilliams, Tim, Hunter, Lawrence, Rademaker, Carin MA, Hivert, Virginie, Ardigò, Diego
Veröffentlicht in Orphanet J Rare Dis (2019)

Barriers to the conduct of randomised clinical trials within all disease areas

von Djurisic, Snezana, Rath, Ana, Gaber, Sabrina, Garattini, Silvio, Bertele, Vittorio, Ngwabyt, Sandra-Nadia, Hivert, Virginie, Neugebauer, Edmund A. M., Laville, Martine, Hiesmayr, Michael, Demotes-Mainard, Jacques, Kubiak, Christine, Jakobsen, Janus C., Gluud, Christian
Veröffentlicht in Trials (2017)

Evaluating the “return on patient engagement initiatives” in medicines research and development: A literature review

von Vat, Lidewij Eva, Finlay, Teresa, Jan Schuitmaker‐Warnaar, Tjerk, Fahy, Nick, Robinson, Paul, Boudes, Mathieu, Diaz, Ana, Ferrer, Elisa, Hivert, Virginie, Purman, Gabor, Kürzinger, Marie‐Laure, Kroes, Robert A., Hey, Claudia, Broerse, Jacqueline E.W.
Veröffentlicht in Health Expect (2019)

Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective

von Dawkins, Hugh J.S., Draghia‐Akli, Ruxandra, Lasko, Paul, Lau, Lilian P.L., Jonker, Anneliene H., Cutillo, Christine M., Rath, Ana, Boycott, Kym M., Baynam, Gareth, Lochmüller, Hanns, Kaufmann, Petra, Le Cam, Yann, Hivert, Virginie, Austin, Christopher P.
Veröffentlicht in Clin Transl Sci (2017)

A systematic literature review of evidence-based clinical practice for rare diseases: what are the perceived and real barriers for improving the evidence and how can they be overco...

von Rath, Ana, Salamon, Valérie, Peixoto, Sandra, Hivert, Virginie, Laville, Martine, Segrestin, Berenice, Neugebauer, Edmund A. M., Eikermann, Michaela, Bertele, Vittorio, Garattini, Silvio, Wetterslev, Jørn, Banzi, Rita, Jakobsen, Janus C., Djurisic, Snezana, Kubiak, Christine, Demotes-Mainard, Jacques, Gluud, Christian
Veröffentlicht in Trials (2017)

Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective

von Austin, Christopher P., Cutillo, Christine M., Lau, Lilian P.L., Jonker, Anneliene H., Rath, Ana, Julkowska, Daria, Thomson, David, Terry, Sharon F., de Montleau, Béatrice, Ardigò, Diego, Hivert, Virginie, Boycott, Kym M., Baynam, Gareth, Kaufmann, Petra, Taruscio, Domenica, Lochmüller, Hanns, Suematsu, Makoto, Incerti, Carlo, Draghia‐Akli, Ruxandra, Norstedt, Irene, Wang, Lu, Dawkins, Hugh J.S.
Veröffentlicht in Clin Transl Sci (2017)