New functionalities in Orphanet for orphan drugs, R&D and marketing authorisations to better serve the rare diseases community

af Hivert, Virginie, Martin, Natalia, Hanauer, Marc, Aymé, Ségolène
Udgivet 2010

Rare diseases research in Europe: an overview based on data from the Orphanet database

af Martin, Natalia, Doulet, Nicolas, Hivert, Virginie, Aymé, Ségolène
Udgivet 2010

Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group

af Gahl, William A., Wong-Rieger, Durhane, Hivert, Virginie, Yang, Rachel, Zanello, Galliano, Groft, Stephen
Udgivet i Orphanet J Rare Dis (2021)

The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases – recommendations of the IRDiRC Data Mining...

af Southall, Noel T, Natarajan, Madhusudan, Lau, Lilian Pek Lian, Jonker, Anneliene Hechtelt, Deprez, Benoît, Guilliams, Tim, Hunter, Lawrence, Rademaker, Carin MA, Hivert, Virginie, Ardigò, Diego
Udgivet i Orphanet J Rare Dis (2019)

Barriers to the conduct of randomised clinical trials within all disease areas

af Djurisic, Snezana, Rath, Ana, Gaber, Sabrina, Garattini, Silvio, Bertele, Vittorio, Ngwabyt, Sandra-Nadia, Hivert, Virginie, Neugebauer, Edmund A. M., Laville, Martine, Hiesmayr, Michael, Demotes-Mainard, Jacques, Kubiak, Christine, Jakobsen, Janus C., Gluud, Christian
Udgivet i Trials (2017)

Evaluating the “return on patient engagement initiatives” in medicines research and development: A literature review

af Vat, Lidewij Eva, Finlay, Teresa, Jan Schuitmaker‐Warnaar, Tjerk, Fahy, Nick, Robinson, Paul, Boudes, Mathieu, Diaz, Ana, Ferrer, Elisa, Hivert, Virginie, Purman, Gabor, Kürzinger, Marie‐Laure, Kroes, Robert A., Hey, Claudia, Broerse, Jacqueline E.W.
Udgivet i Health Expect (2019)

Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective

af Dawkins, Hugh J.S., Draghia‐Akli, Ruxandra, Lasko, Paul, Lau, Lilian P.L., Jonker, Anneliene H., Cutillo, Christine M., Rath, Ana, Boycott, Kym M., Baynam, Gareth, Lochmüller, Hanns, Kaufmann, Petra, Le Cam, Yann, Hivert, Virginie, Austin, Christopher P.
Udgivet i Clin Transl Sci (2017)

A systematic literature review of evidence-based clinical practice for rare diseases: what are the perceived and real barriers for improving the evidence and how can they be overco...

af Rath, Ana, Salamon, Valérie, Peixoto, Sandra, Hivert, Virginie, Laville, Martine, Segrestin, Berenice, Neugebauer, Edmund A. M., Eikermann, Michaela, Bertele, Vittorio, Garattini, Silvio, Wetterslev, Jørn, Banzi, Rita, Jakobsen, Janus C., Djurisic, Snezana, Kubiak, Christine, Demotes-Mainard, Jacques, Gluud, Christian
Udgivet i Trials (2017)

Future of Rare Diseases Research 2017–2027: An IRDiRC Perspective

af Austin, Christopher P., Cutillo, Christine M., Lau, Lilian P.L., Jonker, Anneliene H., Rath, Ana, Julkowska, Daria, Thomson, David, Terry, Sharon F., de Montleau, Béatrice, Ardigò, Diego, Hivert, Virginie, Boycott, Kym M., Baynam, Gareth, Kaufmann, Petra, Taruscio, Domenica, Lochmüller, Hanns, Suematsu, Makoto, Incerti, Carlo, Draghia‐Akli, Ruxandra, Norstedt, Irene, Wang, Lu, Dawkins, Hugh J.S.
Udgivet i Clin Transl Sci (2017)