Characterization of an immunodeficient mouse model of mucopolysaccharidosis type I suitable for preclinical testing of human stem cell and gene therapy

gan Garcia-Rivera, Mayra F., Colvin-Wanshura, Leah E., Nelson, Matthew S., Nan, Zhenhong, Khan, Shaukat A., Rogers, Tyson B., Maitra, Indrani, Low, Walter C., Gupta, Pankaj
Cyhoeddwyd 2007