The involvement of rare disease patient organisations in therapeutic innovation across rare paediatric neurological conditions: a narrative review

por Christina Q. Nguyen, Kristine Alba-Concepcion, Elizabeth E. Palmer, Jackie L. Scully, Nicole Millis, Michelle A. Farrar
Publicado 2022-04-01

Mitochondrial Dysfunction Is an Early Consequence of Partial or Complete Dystrophin Loss in mdx Mice

por Timothy M. Moore, Timothy M. Moore, Amanda J. Lin, Alexander R. Strumwasser, Kevin Cory, Kate Whitney, Theodore Ho, Timothy Ho, Joseph L. Lee, Daniel H. Rucker, Christina Q. Nguyen, Aidan Yackly, Sushil K. Mahata, Sushil K. Mahata, Jonathan Wanagat, Linsey Stiles, Lorraine P. Turcotte, Rachelle H. Crosbie, Rachelle H. Crosbie, Rachelle H. Crosbie, Zhenqi Zhou
Publicado 2020-06-01