The involvement of rare disease patient organisations in therapeutic innovation across rare paediatric neurological conditions: a narrative review

von Christina Q. Nguyen, Kristine Alba-Concepcion, Elizabeth E. Palmer, Jackie L. Scully, Nicole Millis, Michelle A. Farrar
Veröffentlicht 2022-04-01

Mitochondrial Dysfunction Is an Early Consequence of Partial or Complete Dystrophin Loss in mdx Mice

von Timothy M. Moore, Timothy M. Moore, Amanda J. Lin, Alexander R. Strumwasser, Kevin Cory, Kate Whitney, Theodore Ho, Timothy Ho, Joseph L. Lee, Daniel H. Rucker, Christina Q. Nguyen, Aidan Yackly, Sushil K. Mahata, Sushil K. Mahata, Jonathan Wanagat, Linsey Stiles, Lorraine P. Turcotte, Rachelle H. Crosbie, Rachelle H. Crosbie, Rachelle H. Crosbie, Zhenqi Zhou
Veröffentlicht 2020-06-01