The involvement of rare disease patient organisations in therapeutic innovation across rare paediatric neurological conditions: a narrative review

Autor Christina Q. Nguyen, Kristine Alba-Concepcion, Elizabeth E. Palmer, Jackie L. Scully, Nicole Millis, Michelle A. Farrar
Vydáno 2022-04-01

Mitochondrial Dysfunction Is an Early Consequence of Partial or Complete Dystrophin Loss in mdx Mice

Autor Timothy M. Moore, Timothy M. Moore, Amanda J. Lin, Alexander R. Strumwasser, Kevin Cory, Kate Whitney, Theodore Ho, Timothy Ho, Joseph L. Lee, Daniel H. Rucker, Christina Q. Nguyen, Aidan Yackly, Sushil K. Mahata, Sushil K. Mahata, Jonathan Wanagat, Linsey Stiles, Lorraine P. Turcotte, Rachelle H. Crosbie, Rachelle H. Crosbie, Rachelle H. Crosbie, Zhenqi Zhou
Vydáno 2020-06-01