Intracerebroventricular gene therapy that delays neurological disease progression is associated with selective preservation of retinal ganglion cells in a canine model of CLN2 dise...

Autor Whiting, Rebecca E.H., Jensen, Cheryl A., Pearce, Jacqueline W., Gillespie, Lauren E., Bristow, Daniel E., Katz, Martin L.
Vydáno v Exp Eye Res (2016)